Pharmacodynamic results

Tumor-associated Macrophage Depletion, Inhibition, or Repolarization

Last updated: 2026-04-27   Rows: 37 across 35 studies   Outcomes: 19 succeeded / 4 partial / 2 failed / 12 not-assessed (ratio-shift)

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All PBMC tumor TDLN bone marrow ascites skin other
InterventionDiseaseNReportTissueAssayTreg changeResultConfidenceBias & confoundingSourcePMIDDesignDose/scheduleTreg defnReadoutTimepointTiming detailBaselinePostMagnitudeSignificanceDurabilityIntentData sourceNotes
TrabectedinSoft-tissue sarcoma (leiomyosarcoma, liposarcoma)5
Germano G ··· Allavena P
Cancer Cell, 2013
tumorIHC↓ qual.significant reduction
depletion
Lownot-amenable-to-standard-robPMID DOI critique23410977paired-pre-postStandard trabectedinabsolute-countearly-on-treatmentShort on-treatmentMonocyte depletion (including TAMs) observed in treated patientsreportedmechanism-targetedpubmed_abstractGermano 2013 Cancer Cell — landmark paper establishing trabectedin's selective macrophage depletion mechanism. Includes small human/clinical sidecar (small N, ~5 paired biopsies per the preclinical+translational methodology). Low N for clinical row (borderline for N≥3 rule); retained as foundational. Full-text would confirm exact N and tissue-compartment magnitudes.
PF-04136309 (CCR2i) + FOLFIRINOXFOLFIRINOX (chemotherapy)Borderline resectable / locally advanced pancreatic adenocarcinoma39
Nywening TM ··· Linehan DC
Lancet Oncol, 2016
tumorflow↓ qual.significant reduction
depletion
ModerateSeriousPMID PMCID DOI NCT critique27055731treated-vs-untreatedPF-04136309 500 mg BID oral + FOLFIRINOXabsolute-countmid12 weeks of treatment, pre-surgical biopsiesReduction in CCR2+ inflammatory monocytes and TAMs in blood and tumor (per paper's PD analysis)reportedmechanism-targetedpubmed_abstractNywening 2016 Lancet Oncol — landmark CCR2i+FOLFIRINOX pancreatic. Abstract safety/efficacy focused; full PMC text has monocyte/TAM PD data. Abstract-level extraction — numeric values require PMC full-text backfill.
AMG 820 (anti-CSF1R)Advanced solid tumors25
Papadopoulos KP ··· Stephenson J Jr
Clin Cancer Res, 2017
skinIHC↓ qual.significant reduction
depletion
LowModeratePMID DOI critique28655795paired-pre-post0.5 mg/kg weekly or 1.5-20 mg/kg Q2Wabsolute-countmidOn-treatment biopsy'Reduced numbers of skin macrophages' plus pharmacodynamic serum CSF1 increasereportedmechanism-targetedpubmed_abstractPapadopoulos 2017 Clin Cancer Res — AMG 820 first-in-human. Skin used as tissue-macrophage PD surrogate (biopsy of accessible skin, not tumor). Serum CSF1 increase as feedback. No tumor TAM data.
Intratumoral G100 (GLA-SE, TLR4 agonist)Merkel cell carcinoma10
Bhatia S ··· Nghiem P
Clin Cancer Res, 2019
tumorIHC↑ qual.ratio-shift only
repolarization
LowModeratePMID PMCID DOI critique30093453paired-pre-postG100 2-10 μg intratumoral weeklypolarization-marker-shiftearly-on-treatmentPost-injection biopsiesIncreased inflammation in injected tumors; CD8+ and CD4+ T-cell infiltration; activation of immune-related genesreported2 patients recurrence-free at 44+/41+ months; 2 sustained PRs at 33+ monthsmechanism-targetedpubmed_abstractBhatia 2019 Clin Cancer Res — intratumoral G100 in Merkel cell carcinoma phase 1. TLR4 agonism intended to repolarize myeloid TME; abstract-level data are T-cell and gene-expression focused with no direct TAM CD68/CD163 quantification. depletion_success: not-assessed due to no direct macrophage readout.
Hu5F9-G4 (magrolimab) + rituximabRituximab (anti-CD20)Relapsed/refractory DLBCL and follicular lymphoma22
Advani R ··· Smith SM
N Engl J Med, 2018
tumorphago↑ qual.increase
functional only
LowModeratePMID PMCID DOI NCT critique30380386single-arm-descriptive5F9 1 mg/kg prime + 10-30 mg/kg QW maintenance + rituximabphagocytosis-functionmidOn-treatment~100% CD47 receptor occupancy achieved at 30 mg/kg; phagocytosis mechanism inferred from preclinical + CD47 RO; no direct ex vivo phagocytosis assay quantified in abstractreported91% ongoing responses at median follow-up 6.2-8.1 monthsmechanism-targetedpubmed_abstractAdvani 2018 NEJM — landmark CD47 blockade + rituximab in rituximab-refractory NHL. Mechanism is macrophage phagocytosis restoration, but direct ex vivo phagocytosis assay not quantified in abstract. Anemia is on-target phagocytosis signal (depletion of senescent RBCs).
Pexidartinib + paclitaxelPaclitaxel (chemotherapy)Advanced solid tumors (breast cancer expansion)51
Wesolowski R ··· Rugo HS
Ther Adv Med Oncol, 2019
PBMCflow↓ −78.5%significant reduction
depletion
ModerateModeratePMID PMCID DOI critique31258629paired-pre-postPexidartinib dose-escalation (600-2000 mg/d) + paclitaxel 80 mg/m2absolute-countearly-on-treatmentCycle 1CD14dim/CD16+ monocyte levels decreased by 57-100%; plasma CSF-1 increased 1.6- to 53-foldreportedmechanism-targetedpubmed_abstractWesolowski 2019 Ther Adv Med Oncol — pexidartinib + paclitaxel phase 1b. Blood CSF1-dependent CD14dim/CD16+ monocytes pre-specified as CSF1R-depletion PD surrogate (D1 satisfied). Dose-dependent CSF1 feedback rise. No tumor TAM data in abstract.
PF-04136309 (CCR2i) + nab-paclitaxel/gemcitabineNab-paclitaxel + gemcitabineMetastatic pancreatic ductal adenocarcinoma21
Noel M ··· Lowery MA
Invest New Drugs, 2020
PBMCflowmixednull result
null
LowSeriousPMID DOI NCT critique31297636single-arm-descriptivePF-04136309 500 mg BID + nab-pac/gemabsolute-countearly-on-treatmentCycle 1-2No significant change in PD biomarkers; pulmonary toxicity led to study haltn.s.mechanism-targetedpubmed_abstractNoel 2020 Invest New Drugs — PF-04136309 + nab-pac/gem phase 1b. Null-result for CCR2-targeting PD in this chemo backbone; contrast with Nywening 2016 FOLFIRINOX success. Pulmonary toxicity and study halt are critical negative context.
LY3022855 (IMC-CS4, anti-CSF-1R)Metastatic breast cancer (MBC) and castration-resistant prostate cancer (mCRPC)34
Autio KA ··· McArthur HL
Clin Cancer Res, 2020
PBMCflow↓ qual.significant reduction
depletion
LowSeriousPMID DOI NCT critique32847933paired-pre-postLY3022855 monotherapy, dose-escalationabsolute-countearly-on-treatmentDay 8CD14dim CD16bright monocytes decreased at day 8; circulating CSF-1 increasedreportedmechanism-targetedpubmed_abstractAutio 2020 Clin Cancer Res — LY3022855 monotherapy. Blood CD14dim CD16bright monocyte pre-specified PD (D1 satisfied). No tumor CD68 quantification in abstract.
Pexidartinib (PLX3397)Relapsed/refractory pediatric leukemias and solid tumors16
Boal LH ··· Kaplan RN
Clin Cancer Res, 2020
PBMCflow↓ qual.significant reduction
depletion
LowModeratePMID PMCID DOI critique32943455single-arm-descriptive400, 600, 800 mg/m2 daily, 28-day cyclesabsolute-countearly-on-treatmentCycle 1Plasma MCSF rise; absolute monocyte count decreasereportedOne mesothelioma patient SD at C49+mechanism-targetedpubmed_abstractBoal 2020 Clin Cancer Res — pediatric pexidartinib phase 1. Blood monocyte count + MCSF as pre-specified CSF1R PD surrogate.
AMG 820 + pembrolizumabPembrolizumab (anti-PD-1)Advanced solid tumors (pancreatic, CRC, NSCLC)116
Razak AR ··· Papadopoulos KP
J Immunother Cancer, 2020
PBMCflow↓ qual.significant reduction
depletion
ModerateModeratePMID PMCID DOI NCT critique33046621paired-pre-postAMG 820 1100 mg or 1400 mg IV + pembrolizumab 200 mg Q3Wabsolute-countearly-on-treatmentOn-treatmentReduction in CSF1-dependent CD16-expressing monocytes; accumulation of serum CSF1 and IL-34reportedmechanism-targetedpubmed_abstractRazak 2020 JITC — AMG 820 + pembrolizumab. PD target engagement (CD16+ monocyte reduction, CSF1/IL-34 feedback) achieved but not translated to clinical benefit — a PD/efficacy disconnect.
AMG 820 + pembrolizumabPembrolizumab (anti-PD-1)Advanced solid tumors116
Razak AR ··· Papadopoulos KP
J Immunother Cancer, 2020
tumorIHC↑ qual.ratio-shift only
repolarization
ModerateModeratePMID PMCID DOI NCT critique33046621paired-pre-postAMG 820 1100 mg + pembrolizumab 200 mg Q3WothermidOn-treatment biopsyIncreased PD-L1 expression and increased CD4 and CD8 cells in tumor biopsiesreportedmechanism-targetedpubmed_abstractSame trial as above (Razak 2020). Tumor compartment data is T-cell/PD-L1 centric; direct tumor CD68/CD163 TAM counts not reported. Row retained as paired PD endpoint from the same trial, with readout_type: other and depletion_success: not-assessed since no direct TAM quantification.
Emactuzumab + selicrelumab (CD40 agonist)Selicrelumab (CD40 agonist, RO7009789)Advanced solid tumors37
Machiels JP ··· Cassier P
J Immunother Cancer, 2020
PBMCflow↓ qual.significant reduction
depletion
ModerateModeratePMID PMCID DOI NCT critique33097612paired-pre-postEmactuzumab 1000 mg + selicrelumab 16 mg Q3Wabsolute-countearly-on-treatmentOn-treatmentReduction of CD14dim CD16bright monocytes; increase of Ki67+ CD8+ T cells; decrease of B cellsreportedmechanism-targetedpubmed_abstractMachiels 2020 JITC — emactuzumab + selicrelumab. Blood CD14dim CD16bright monocytes are pre-specified CSF1R-depletion PD surrogate (D1 satisfied). N=37 is estimate from reported 40.5% SD rate — actual N to verify in full text.
Emactuzumab (RG7155, anti-CSF1R)Diffuse-type tenosynovial giant-cell tumor (dTGCT)36
Cassier PA ··· Delord JP
Eur J Cancer, 2020
tumorIHC↓ qual.significant reduction
depletion
ModerateModeratePMID DOI NCT critique33161240paired-pre-post1000 mg IV every 2 weeks (optimal biological dose)absolute-countmidOn-treatment biopsy (post-cycle)'Substantial decrease' in CSF1R+ and CD68/CD163+ macrophages in on-treatment biopsies (36 patients with paired tissue)reported2-year ORR 64%; responses durable during maintained dosingmechanism-targetedpubmed_abstractCassier 2020 EJC long-term update of emactuzumab in dTGCT. On-target macrophage depletion in synovial TGCT tissue (disease driven by CSF1/CSF1R axis). Abstract reports qualitative 'substantial decrease' in CSF1R+ and CD68/CD163+ macrophages; full-text would quantify. Landmark example of clinical TAM depletion with durable efficacy.
LY3022855 (anti-CSF-1R)Advanced solid tumors52
Dowlati A ··· Wesolowski R
Invest New Drugs, 2021
PBMCflow↓ qual.significant reduction
depletion
LowModeratePMID DOI NCT critique33624233paired-pre-postDose-escalation, 100 mg IV weekly (RP2D)absolute-countearly-on-treatmentMulti-timepoint post-doseTAMs and CD14dim CD16bright monocyte levels decreased with treatment; serum CSF-1 and IL-34 increasedreportedmechanism-targetedpubmed_abstractDowlati 2021 Invest New Drugs — LY3022855 monotherapy phase 1. Abstract reports TAMs (unclear whether tumor or blood monocyte surrogate) decreased; PD engagement achieved without clinical efficacy.
LY3022855 + durvalumab or tremelimumabDurvalumab (anti-PD-L1) or tremelimumab (anti-CTLA-4)Advanced solid tumors (NSCLC, ovarian cohorts)72
Falchook GS ··· Peterson DA
Invest New Drugs, 2021
PBMCmixednull result
null
LowModeratePMID DOI NCT critique33852104paired-pre-postLY3022855 100 mg QW + durvalumab 750 mg Q2Wotherearly-on-treatmentCycle 1-2mechanism-targetedpubmed_abstractFalchook 2021 Invest New Drugs — LY3022855 + durvalumab/tremelimumab phase 1a/1b. Abstract is PK-focused with no explicit macrophage/monocyte PD data. Retained as companion row to Dowlati 2021 for intervention-class coverage; no specific TAM PD readout reported in abstract.
Bexmarilimab (FP-1305, anti-CLEVER-1)Heavily pre-treated metastatic cancer30
Virtakoivu R ··· Hollmén M
Clin Cancer Res, 2021
PBMCCyTOF↑ qual.repolarized
repolarization
HighLowPMID PMCID DOI NCT critique34078651paired-pre-postDose-finding 0.3-10 mg/kg IVpolarization-marker-shiftearly-on-treatmentPost-doseBlood monocytes exhibited proinflammatory phenotypic switch; suppressed nuclear lipid signaling; impaired vacuolar ATPase-mediated endosomal acidification; peripheral T-cell activationreportedmechanism-targetedpubmed_abstractVirtakoivu 2021 Clin Cancer Res — bexmarilimab Part I (n=30) of MATINS. Peripheral myeloid reprogramming signal captured via CyTOF (D1 + D7 satisfied). Multi-dimensional evidence supports repolarization.
Neoadjuvant selicrelumab (CD40 agonist) ± chemotherapyGemcitabine + nab-paclitaxel (in subset)Resectable pancreatic ductal adenocarcinoma16
Byrne KT ··· Vonderheide RH
Clin Cancer Res, 2021
tumorIHC↓ qual.significant reduction
ratio only
ModerateModeratePMID PMCID DOI critique34112709single-arm-descriptiveSelicrelumab 16 mg IV, preoperativeratio-M1-to-M2midSurgical resection ~2-4 weeks after doseM2-like TAMs fewer in selicrelumab-treated tumors vs controls; tumor fibrosis reduced; intratumoral DCs more mature; T cells more activereportedmechanism-targetedpubmed_abstractByrne 2021 Clin Cancer Res — neoadjuvant selicrelumab in resectable PDAC window-of-opportunity. M2-like TAM reduction + DC maturation + T-cell activation is coherent repolarization/ratio-shift signal. Abstract qualitative; full text has numeric IHC data.
APX005M (sotigalimab) + cabiralizumab + nivolumabAPX005M (CD40 agonist) + nivolumab (anti-PD-1); cabiralizumab is anti-CSF1RAdvanced melanoma, NSCLC, RCC (anti-PD-1 resistant)26
Weiss SA ··· Kluger HM
Clin Cancer Res, 2021
PBMCmixed↑ qual.ratio-shift only
repolarization
ModerateModeratePMID PMCID DOI NCT critique34140403paired-pre-postAPX005M 0.3 mg/kg + cabiralizumab 4 mg/kg + nivolumab 240 mg Q2Wpolarization-marker-shiftearly-on-treatment4 hours post-infusionPro-inflammatory cytokine upregulation at 4h; CD40 and MCSF serum increase post-therapyreportedmechanism-targetedpubmed_abstractWeiss 2021 Clin Cancer Res — dual macrophage-polarizing therapy (CD40 agonist + CSF1Ri) + nivo in ICI-resistant disease. PD engagement but poor clinical activity. Macrophage-polarization surrogates captured; no direct tumor TAM count readout in abstract.
Pexidartinib + sirolimusSirolimus (mTOR inhibitor)Advanced sarcoma (including dedifferentiated/pleomorphic subtypes)18
Manji GA ··· Schwartz GK
Clin Cancer Res, 2021
tumorIHC↓ qual.significant reduction
depletion
LowSeriousPMID PMCID DOI NCT critique34321280paired-pre-postPexidartinib 1000 mg + sirolimus 2 mg daily (RP2D)absolute-countmidOn-treatment biopsy'Decreased proportion of activated M2 macrophages within tumor samples with treatment'reportedmechanism-targetedpubmed_abstractManji 2021 Clin Cancer Res — pexidartinib + sirolimus in sarcoma. Qualitative M2 macrophage reduction in tumor IHC; no absolute count values in abstract.
MIW815 (ADU-S100), intratumoral STING agonistAdvanced/metastatic solid tumors and lymphomas47
Meric-Bernstam F ··· Luke JJ
Clin Cancer Res, 2022
tumormixed↑ qual.ratio-shift only
repolarization
ModerateModeratePMID DOI critique34716197paired-pre-postIntratumoral 50-6400 μg weekly, 3-weeks-on/1-offpolarization-marker-shiftearly-on-treatmentOn-treatment biopsyEvidence of systemic immune activation; inflammatory cytokines elevated; T-cell clonal expansion; tumor biopsy RNA expression changesreportedmechanism-targetedpubmed_abstractMeric-Bernstam 2022 Clin Cancer Res — MIW815 (ADU-S100) intratumoral STING phase 1. STING-driven type-I IFN mechanism is intended to repolarize myeloid TME; abstract documents immune activation but not direct TAM count/polarization. Full-text required for specific myeloid PD.
Emactuzumab + atezolizumabAtezolizumab (anti-PD-L1)Advanced solid tumors (ICB-naive UBC, melanoma; ICB-experienced NSCLC, UBC, melanoma)221
Gomez-Roca C ··· Marabelle A
J Immunother Cancer, 2022
tumormIFmixednonsignificant trend
depletion
HighModeratePMID PMCID DOI NCT critique35577503paired-pre-postEmactuzumab 1000 mg + atezolizumab 1200 mg Q3Wabsolute-countmidOn-treatment biopsyTAM reduction observed but 'less TAM reduction in ICB-experienced compared with ICB-naïve patients'; persistence of a TAM subpopulation associated with CD8+ TIL increasereportedmechanism-targetedpubmed_abstractGomez-Roca 2022 JITC — emactuzumab + atezo phase 1b. Key observation: TAM reduction is less complete in ICB-experienced patients; a persistent TAM subpopulation correlates with CD8 TIL increase. Interpreted as repolarization signal alongside depletion. Abstract-level; quantitative magnitudes require full-text.
Axatilimab (SNDX-6352, anti-CSF1R)Chronic graft-versus-host disease (cGVHD)40
Kitko CL ··· Lee SJ
J Clin Oncol, 2023
PBMCflow↓ qual.significant reduction
depletion
ModerateModeratePMID PMCID DOI NCT critique36459673single-arm-descriptive3 mg/kg IV Q4W (RP2D)polarization-marker-shiftmidCycle 7 day 1ORR 50% at C7D1 (primary endpoint); ORR 82% across first 6 cyclesreportedDurable clinical responses; 58% significant symptom improvement per Lee Symptom Scalemechanism-targetedpubmed_abstractKitko 2023 JCO — axatilimab in cGVHD phase 1/2. Not a cancer indication but the best clinical proof of CSF1R-dependent macrophage-driven disease modulation in humans. Kept as in-scope because CSF1R macrophage ablation is the mechanistic target. No direct tumor TAM counts (not applicable); clinical-response magnitude used as PD surrogate.
Magrolimab + azacitidineAzacitidineHigher-risk MDS95
Sallman DA ··· Daver NG
J Clin Oncol, 2023
bone-marrowphago↑ qual.increase
functional only
LowModeratePMID PMCID DOI NCT critique36888930single-arm-descriptiveMagrolimab IV + aza standardphagocytosis-functionmidOn-treatmentCR 33%, ORR 75%, mDOR 11.1 mo; mPFS 11.6 mo; TP53-mut CR 40%reportedMedian duration of CR 11.1 mo; mDOR 9.8 momechanism-targetedpubmed_abstractSallman 2023 JCO — magrolimab + aza in higher-risk MDS. CD47 blockade restores macrophage phagocytosis of MDS blasts (preclinical mechanism). Direct phagocytosis measurement not in abstract. Phase 3 ENHANCE (NCT04313881) subsequently failed (2024) — include for PD/efficacy context.
Eganelisib (IPI-549) ± nivolumabNivolumab (anti-PD-1) in combo cohortAdvanced solid tumors (melanoma, HNSCC, others)219
Hong DS ··· Wolchok JD
Clin Cancer Res, 2023
PBMCmixednull result
null
ModerateModeratePMID PMCID DOI NCT critique37000164paired-pre-postMonotherapy 10-60 mg QD; combination 20-40 mg QD + nivolumabpolarization-marker-shiftearly-on-treatmentCycle 1-2PD-activity reported but abstract does not specify TAM/myeloid PD magnitudemechanism-targetedpubmed_abstractHong 2023 Clin Cancer Res — MARIO-1 eganelisib mono/combo phase 1. Abstract emphasizes safety and clinical activity; no quantitative TAM PD in abstract. MARIO-3 (O'Connell 2024) contains the TAM reprogramming data (captured below).
SEA-CD40 (non-fucosylated CD40 agonist)Advanced solid tumors and lymphoma67
Coveler AL ··· Grilley-Olson JE
J Immunother Cancer, 2023
PBMCmixed↑ qual.nonsignificant trend
repolarization
ModerateModeratePMID PMCID DOI NCT critique37385724paired-pre-postDose-escalation, 10-30 μg/kg selectedpolarization-marker-shiftearly-on-treatment21-day cyclesDose-dependent cytokine induction; activation and trafficking of innate and adaptive immune cellsreportedmechanism-targetedpubmed_abstractCoveler 2023 JITC — SEA-CD40 phase 1. Non-fucosylated Fc increases ADCP by FcγR-enhanced binding. PD data is blood cytokine/immune-activation focused; no direct tumor TAM quantification in abstract.
Bexmarilimab (FP-1305, anti-CLEVER-1)Treatment-refractory advanced solid tumors138
Rannikko JH ··· Bono P
Cell Rep Med, 2023
tumorscRNA↑ qual.repolarized
repolarization
ModerateModeratePMID PMCID DOI NCT critique38056464paired-pre-postDose-escalation 0.3-10 mg/kg IVpolarization-marker-shiftmidOn-treatment biopsiesMacrophage activation signatures increase on-treatment; disease control correlated with high pre-treatment intratumoral CLEVER-1 positivity and increasing on-treatment serum IFNγreportedmechanism-targetedpubmed_abstractRannikko 2023 Cell Rep Med — MATINS first-in-human bexmarilimab. The MATINS trial (Part I+II). Bexmarilimab converts immunosuppressive TAMs to activated phenotype; direct phagocytosis/function changes documented. Part I (n=30) reported separately in Virtakoivu 2021 (below).
Neoadjuvant sotigalimab + chemoradiationChemoradiationLocally advanced esophageal/gastroesophageal junction adenocarcinoma6
Soto M ··· Keenan BP
Cancer Res Commun, 2024
tumorscRNA↑ qual.repolarized
repolarization
ModerateModeratePMID PMCID DOI critique38181044paired-pre-postSotigalimab (APX005M) IV pre-CRTscRNA-cluster-shiftearly-on-treatmentPost initial sotigalimab dose, pre-CRTIncreased antigen presentation; altered myeloid metabolism; elevated T-cell activation/cytotoxicity; reduced TME Tregsreportedmechanism-targetedpubmed_abstractSoto 2024 Cancer Res Commun — neoadjuvant sotigalimab + CRT in E/GEJ cancer. Deep TIME-profiling via scRNA-seq + CITEseq + MIBI. Myeloid metabolism + antigen-presentation shift is a high-quality repolarization signal on multi-marker evidence.
PY314 (anti-TREM2) + pembrolizumabPembrolizumab (anti-PD-1)Advanced renal cell carcinoma (ICI-refractory)17
Beckermann KE ··· Rini BI
Invest New Drugs, 2024
tumorIHCnull result
null
LowModeratePMID DOI NCT critique38372949single-arm-descriptivePY314 + pembroabsolute-countmidRECISTmPFS 1.4 mo; 1 PR, 4 SDmechanism-targetedpubmed_abstractBeckermann 2024 Invest New Drugs — PY314 + pembro in CPI-refractory RCC. Abstract is PK/safety focused; no TAM PD magnitude. Clinical activity poor — TREM2 targeting does not overcome prior CPI resistance in RCC.
Metronomic trabectedin + low-dose cyclophosphamide (TARMIC)Low-dose cyclophosphamideAdvanced soft-tissue sarcoma28
Sun CM ··· Italiano A
Mol Cancer, 2024
tumorIHC↓ qual.nonsignificant trend
depletion
LowSeriousPMID PMCID DOI NCT critique38374062paired-pre-postMetronomic trabectedin + low-dose cycloabsolute-countearly-on-treatment4 weeks post-treatmentDecreased CD68+CD163+ macrophages in tumor biopsies of 9/28 patients (32%); CD8+ T-cell increase in 11/28 (39%); composite positive immune response in up to 57%reportedmechanism-targetedpubmed_abstractSun 2024 TARMIC Mol Cancer — metronomic trabectedin + cyclo in STS. 32% of patients show tumor CD68+CD163+ reduction — a partial-response signal. Compelling ratio-shift (9/28 TAM ↓ with 11/28 CD8 ↑) and PFS correlate.
Eganelisib + atezolizumab + nab-paclitaxelAtezolizumab (anti-PD-L1) + nab-paclitaxel (chemotherapy)Metastatic triple-negative breast cancer (TNBC)12
O'Connell BC ··· Peluso S
J Immunother Cancer, 2024
tumorscRNA↑ qual.repolarized
repolarization
ModerateModeratePMID PMCID DOI NCT critique39214650paired-pre-postEganelisib 30 mg or 40 mg QD + atezo + nab-pacscRNA-cluster-shiftmidOn-treatment biopsyGene signatures of TAM reprogramming, immune activation, and ECM reorganization detected; associated with longer PFSreportedmechanism-targetedpubmed_abstractO'Connell 2024 JITC — MARIO-3 eganelisib + atezo + nab-pac TNBC. Paired biopsy multiplex IF + GeoMx spatial transcriptomics; TAM reprogramming (M2→M1) is the intended mechanism. Repolarization row; multi-marker evidence supports `succeeded`. N=12 refers to spatial transcriptomics paired-biopsy subset; 18 for PD-L1 IHC subset.
IO-108 (anti-LILRB2) ± pembrolizumabPembrolizumab (in combination arm)Advanced solid tumors25
Taylor MH ··· Patel MR
J Immunother Cancer, 2024
tumormixed↑ qual.ratio-shift only
repolarization
ModerateModeratePMID PMCID DOI NCT critique39567210paired-pre-postIO-108 dose-escalation Q3Wpolarization-marker-shiftmidOn-treatment biopsyPD gene expression changes reflecting increased tumor T-cell infiltration; baseline TIS predicts responsereportedOne CR >2 years (Merkel cell carcinoma, monotherapy)mechanism-targetedpubmed_abstractTaylor 2024 JITC — IO-108 anti-LILRB2 phase 1. Tumor transcriptomic PD (increased T-cell infiltration) is intended surrogate for myeloid reprogramming but direct macrophage cluster analysis not reported in abstract.
PY314 (anti-TREM2)Platinum-resistant ovarian cancer16
Yeku OO ··· Winer I
J Immunother Cancer, 2025
tumorIHC↓ qual.ratio-shift only
depletion
ModerateModeratePMID PMCID DOI critique40081941single-arm-descriptivePY314 dose-escalation Q3Wabsolute-countmidRECIST assessment every 6 weeksMechanism: PY314 'depletes tumor-associated macrophages'; abstract does not quantify tumor CD68/TREM2 changemechanism-targetedpubmed_abstractYeku 2025 JITC — PY159 and PY314 (TREM1 agonist + TREM2 antagonist) parallel arms in platinum-resistant ovarian. Abstract emphasizes mechanism and clinical outcomes; direct tumor TAM quantification not in abstract.
PY159 (TREM1 agonist antibody)Platinum-resistant ovarian cancer17
Yeku OO ··· Winer I
J Immunother Cancer, 2025
tumorIHC↑ qual.ratio-shift only
repolarization
ModerateModeratePMID PMCID DOI critique40081941single-arm-descriptivePY159 dose-escalation Q3Wpolarization-marker-shiftmidRECIST every 6 weeksMechanism: PY159 'reprograms immunosuppressive intratumoral myeloid cells'; abstract does not quantifymechanism-targetedpubmed_abstractYeku 2025 JITC PY159 arm. Paired with PY314 row above. Classified as other-repolarizing since PY159 is a myeloid-reprogramming agonist not fitting the 12 canonical families exactly.
BMS-813160 (CCR2/5 dual antagonist) + nivolumab + gemcitabine + nab-paclitaxelNivolumab + gemcitabine + nab-paclitaxelBorderline resectable / locally advanced pancreatic cancer32
Grierson PM ··· Lim KH
Clin Cancer Res, 2025
tumorIHC↓ qual.significant reduction
depletion
ModerateModeratePMID PMCID DOI NCT critique40125795randomized-controlledBMS-813160 + nivo + GnP neoadjuvant, 4 cyclesabsolute-countmidAfter 4 cycles neoadjuvantIntratumoral monocytes and macrophages decreased; T-cell proliferation and effector genes enhancedreportedmechanism-targetedpubmed_abstractGrierson 2025 Clin Cancer Res — BMS-813160 + nivo + GnP neoadjuvant PDAC. Randomized-controlled design with GnP-alone control (N=8). Clear intratumoral TAM reduction + T-cell activation + clinical activity.
Magrolimab + azacitidine + venetoclaxAzacitidine + venetoclaxAML (first-line and R/R)106
Daver N ··· Abbas HA
Clin Cancer Res, 2025
bone-marrowphago↑ qual.increase
functional only
LowModeratePMID PMCID DOI critique40198272single-arm-descriptiveMagrolimab + aza + ven standardphagocytosis-functionmidOn-treatment1L CRc 63% (49% TP53-mut, 90% TP53 wt); R/R CRc 29%reported1L mEFS 6.6 mo, mOS 9.8 momechanism-targetedpubmed_abstractDaver 2025 Clin Cancer Res — aza+ven+magrolimab in AML. CD47-phagocytosis mechanism; no direct ex vivo phagocytosis in abstract. Context: broader magrolimab program halted after sepsis/anemia signals.
Bexmarilimab + azacitidineAzacitidineMDS and R/R AML33
Kontro M ··· Daver N
Lancet Haematol, 2025
bone-marrowmixedratio-shift only
repolarization
LowModeratePMID DOI NCT critique40449509single-arm-descriptiveBexmarilimab 1, 3, or 6 mg/kg IV weekly + aza standardpolarization-marker-shiftmidCycle 1-cycle 6ORR 45% (15/33); MTD not reachedreportedMedian follow-up 6.2 monthsmechanism-targetedpubmed_abstractKontro 2025 Lancet Haematol — bexmarilimab + aza in MDS/AML phase 1. Marrow-macrophage reprogramming is the intended mechanism but direct marrow macrophage PD data not in abstract. Included for intervention coverage and the first hematologic CLEVER-1 trial.
Evorpacept (ALX148) + lenalidomide + rituximabLenalidomide + rituximabRelapsed/refractory B-cell NHL (mostly indolent)20
Strati P ··· Flowers CR
Clin Cancer Res, 2025
tumormIF↑ qual.repolarized
expansion + repol
LowModeratePMID PMCID DOI NCT critique40729376paired-pre-postEvorpacept 30 or 60 mg/kg + lenalidomide 20 mg + rituximab 375 mg/m2polarization-marker-shiftearly-on-treatmentEnd of cycle 1Significant increase in T cells and macrophages; anti-tumoral macrophage pathways upregulatedreportedMedian follow-up 28 mo; 2-yr PFS 69%mechanism-targetedpubmed_abstractStrati 2025 Clin Cancer Res — evorpacept + len + rituximab in R/R B-NHL. Rare example of intratumoral macrophage expansion toward anti-tumoral (M1-like) polarization. Assigned expansion-with-repolarization mechanism.